RNA-BASED THERAPY

  • RNA drugs potentially allow precise silencing or activation of genes
     

  • Advanced antisense RNA drugs enable precise control of gene expression, addressing diseases such as Huntington’s, DMD and SMA
     

  • Very rapid bioinformatics-based drug design cycles

THERAPEUTIC AREAS

  • Virology

  • Gain-of-function disorders

  • Liver disorders

  • Autoimmune disease