top of page

GENE THERAPY

  • Gene therapies allow treatment of previously unapproachable genetic and metabolic diseases with significant unmet medical needs
     

  • Gene editing, while earlier in development than current gene therapies, potentially allows treatment of a wider disease range

THERAPEUTIC AREAS

  • All monogenic disorders

  • Gain-of-function disorders 

  • Oncology

  • Autoimmune disorders

bottom of page